Muscular Dystrophy News

April 8, 2021April 8, 2021

Keisha Greaves Named MDA’s 2021 National Goodwill Ambassador

The Muscular Dystrophy Association (MDA) has named Keisha Greaves, a fashion entrepreneur and neuromuscular disease advocate from Cambridge, Massachusetts, as its latest National Ambassador. “I have been involved with MDA because ... Read more

April 6, 2021April 6, 2021

Audentes Becomes Astellas Gene Therapies, Will Advance MD Treatments

Muscular Dystrophy News

Following its acquisition last year by Astellas Pharma, Audentes Therapeutics now has become Astellas Gene Therapies. Named a Gene Therapy Center of Excellence, it will work to advance the development ... Read more

April 1, 2021April 1, 2021

Flavocoxid Well-tolerated, Lessens Inflammation in Small DMD Trial

Muscular Dystrophy News

Flavocoxid was well-tolerated and lessened inflammation in a small clinical trial involving boys with Duchenne muscular dystrophy (DMD). Researchers said these results support Flavocoxid’s further investigation as a potential DMD ... Read more

March 30, 2021March 30, 2021

Cost of Rare Diseases in US? Nearly $1 Trillion in 2019, EveryLife Foundation Finds

Muscular Dystrophy News

As anyone affected by a rare disease knows, treating the illness while trying to go about everyday life is an expensive undertaking. But exactly how expensive — in terms of ... Read more

March 25, 2021March 25, 2021

Second Phase 3 Study of Pamrevlumab Recruiting Boys With DMD

Muscular Dystrophy News

FibroGen has begun a second Phase 3 clinical trial of pamrevlumab, given with corticosteroids, among boys with Duchenne muscular dystrophy (DMD) who are able to walk. The trial, LELANTOS-2 (NCT04632940), ... Read more

March 24, 2021March 25, 2021

#MDA2021 – Long-term Vamorolone Slowed Disease Progression in DMD Boys

Muscular Dystrophy News

Editor’s note: The Muscular Dystrophy News Today team is providing in-depth coverage of the 2021 MDA Virtual Clinical and Scientific Conference, March 15–18. Go here to read the latest stories from the conference. Long-term ... Read more

March 24, 2021March 24, 2021