Muscular Dystrophy News

July 19, 2019July 19, 2019

European Initiative Targets Diagnosis, Treatment of Rare Diseases

This post was originally published on this siteThis post was originally published on this site A new international consortium based in Paris, and ... Read more

July 19, 2019July 19, 2019

Cell Therapy CAP-1002 Improves Muscle, Lung Function in Boys with DMD, Interim Data Show

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site CAP-1002, Capricor Therapeutics’ investigational cell therapy for Duchenne ... Read more

July 18, 2019July 18, 2019

‘Disabled’ vs. ‘Having a Disability’: Debating the Power of Words

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site In the disability community, which is as diverse ... Read more

July 17, 2019July 17, 2019

Pfizer’s Gene Therapy Holds Promise in Treatment of DMD, Early Data Show

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site PF-06939926, Pfizer‘s experimental gene therapy for the treatment ... Read more

July 15, 2019July 17, 2019

UberWAV Is the Next Best Thing for Accessible Transportation

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site I discovered something different about Washington, D.C. when ... Read more

July 15, 2019July 15, 2019

Exondys 51 Superior to Glucocorticoids in Preserving Respiratory Health of Duchenne Boys, Analysis Shows

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site Treatment with Exondys 51 (eteplirsen) significantly slows respiratory decline in ... Read more

July 12, 2019July 12, 2019

$500K Gift to MDA Summer Camp Will Honor Robert Bennett Legacy

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site For more than 20 years, Robert (Bob) Bennett ... Read more

July 11, 2019July 11, 2019

The Speak Foundation Speaks Loudly: A Prelude to September in Chicago

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site I recently attended The Speak Foundation’s 11th Annual ... Read more

July 10, 2019July 10, 2019

Macedonian Gaucher Activist Publicizes Plight of Rare Disease Patients

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site The challenges Vesna Aleksovska faced when she decided ... Read more

July 10, 2019July 10, 2019

Potential DMD Treatment, Pamrevlumab, Helps to Preserve Lung, Heart and Upper Limb Function in Youth, Early Trial Data Show

Muscular Dystrophy News

This post was originally published on this siteThis post was originally published on this site Early trial data supports the potential of FibroGen‘s ... Read more