Huntington’s Disease News

January 11, 2022January 11, 2022

Austedo Adherence Rates Higher Than Xenazine’s, US Study Finds

Huntington's Disease News

People with Huntington’s disease are more likely to take Austedo (deutetrabenazine) as directed, compared with the similar medication Xenazine (tetrabenazine), according to a new study. The study also found lower ... Read more

January 4, 2022January 4, 2022

Top 10 Huntington’s Disease Stories of 2021

Huntington's Disease News

Throughout 2021, Huntington’s Disease News brought you daily coverage of the latest scientific findings, treatment developments, and clinical trials related to Huntington’s disease. As a reminder of what mattered most to ... Read more

December 28, 2021December 28, 2021

Branaplam on FDA’s Fast Track; Phase 2 Trial Now Enrolling

Huntington's Disease News

The experimental oral medication branaplam (LMI070) has been granted fast track designation by the U.S. Food and Drug Administration (FDA) as a potential treatment for Huntington’s disease, according to an ... Read more

December 21, 2021December 21, 2021

AMT-130 Well-tolerated Up to a Year in First Two Patients Treated

Huntington's Disease News

AMT-130, an investigational gene therapy for the treatment of Huntington’s disease, was overall well-tolerated up to a year after treatment in the first patients to receive the therapy in a ... Read more

December 14, 2021December 14, 2021

Valbenazine Eases Chorea in Trial; FDA Submission Expected Next Year

Huntington's Disease News

Treatment with valbenazine significantly lessened chorea — a motor symptom characterized by jerky, unpredictable, and involuntary movements — in people with Huntington’s disease in the Phase 3 clinical trial KINECT-HD, ... Read more

December 7, 2021December 7, 2021

KINECT-HD2 Study of Oral Valbenazine for Chorea Enrolling

Huntington's Disease News

The Huntington Study Group is seeking 30 patients to join KINECT-HD2, an open-label study of oral valbenazine capsules for chorea, or jerky involuntary movements, in Huntington’s disease, a press release ... Read more

November 30, 2021November 30, 2021

US Trial of Gene Therapy AMT-130 Enrolling High-dose Patient Group

Huntington's Disease News

A Phase 1/2 clinical trial testing uniQure’s potential gene therapy AMT-130 in people with Huntington’s disease can continue enrollment, according to a positive review by the study’s independent data safety monitoring board ... Read more

November 23, 2021November 23, 2021

FDA Places Prilenia’s Oral Pridopidine on Fast Track

Huntington's Disease News

The U.S. Food and Drug Administration (FDA) has given fast track designation to Prilenia Therapeutics’ pridopidine as a potential oral treatment for Huntington’s disease. This designation is given to therapies ... Read more

November 16, 2021November 16, 2021

HDSA’s 7th Annual Freeze HD Event Raises $211K to Help Families

Huntington's Disease News

Celebrities turned out in force — albeit virtually — to support the 7th Annual Freeze HD event, hosted by the Huntington’s Disease Society of America (HDSA), which raised more than $211,000 ... Read more

November 9, 2021November 9, 2021

Hereditary Disease Foundation Awards Prizes to Leaders in Research

Huntington's Disease News

Two scientists investigating Huntington’s disease have been awarded prizes by the Hereditary Disease Foundation, recognizing their leadership in disease research. The Leslie Gehry Brenner Prize for Innovation in Science was ... Read more

November 2, 2021November 2, 2021

Enrollment Now Complete for PROOF-HD Trial of Oral Pridopidine

Huntington's Disease News

A Phase 3 clinical trial investigating the efficacy and safety of oral pridopidine for those with early stage Huntington’s disease is now underway at more than 50 clinical sites in the ... Read more

October 26, 2021October 26, 2021

Bladder, Bowel, Sexual Problems Common, Patients Report

Huntington's Disease News

Frequent bladder, bowel, and sexual problems were reported by people with Huntington’s disease, a study reveals. Recommended Reading October 13, 2021 Columns by B.J. Viau These 5 Changes Are Needed ... Read more

October 19, 2021October 19, 2021

Global Genes, Diversity Coalition Team Up to Advance Health Equity

Huntington's Disease News

Global Genes has partnered with the Rare Disease Diversity Coalition (RDDC) to advance health equity for rare disease patients and caregivers in underrepresented communities of color. “For rare disease patients, ... Read more

October 19, 2021October 19, 2021

FDA Grants Orphan Drug Status to SOM Biotech’s Chorea Therapy

Huntington's Disease News

The U.S. Food and Drug Administration (FDA) has granted an orphan drug designation to SOM3355, an investigational treatment for chorea, or involuntary jerky movements, associated with Huntington’s disease, its developer ... Read more

October 12, 2021October 12, 2021

Rare Disease Diversity Coalition Awards $600K to Combat Disparities

Huntington's Disease News

The Rare Disease Diversity Coalition (RDDC) awarded $600,000 in grants to ease the disparities faced by rare disease patients of color. These Impact Rare Disease Solution grants will go five RDDC ... Read more