COVID-19 News

November 30, 2020November 30, 2020

New Mouse Study Will Investigate EmtinB as Post-COVID Fibrosis Treatment

NeuroScientific Biopharmaceuticals, the Institute for Respiratory Health, and the University of Western Australia (UWA) have initiated a preclinical study assessing the potential of EmtinB and other related, lab-made compounds to ... Read more

November 30, 2020November 30, 2020

FDA Requests More Data to Support LIQ861’s Potential Approval for PAH

COVID-19 News, Pulmonary Hypertension News

The U.S. Food and Drug Administration (FDA) determined that additional data is required to support the potential approval of LIQ861, Liquidia Technologies’ investigational inhaled formulation of treprostinil, for the treatment ... Read more

November 26, 2020November 26, 2020

Survey Finds COVID-19 Disrupted Care, Well-Being of Rare Disease Patients in Europe

COVID-19 News, Pompe Disease News

The first wave of COVID-19 in Europe severely disrupted access to care and raised stress and anxiety in people with rare diseases, negatively affecting their health and well-being, according to a ... Read more

November 25, 2020

COVID-19: Your Weekly Roundup of Key Developments

COVID-19 News

AstraZeneca vaccine candidate shows promise An interim analysis of AZD1222, the COVID-19 vaccine candidate being developed by AstraZeneca and the University of Oxford, met its primary goal, finding the vaccine ... Read more

November 25, 2020November 25, 2020

Cure SMA Offering Free Masks, Other COVID-19 Equipment to Patients

COVID-19 News, SMA News Today

Cure SMA is offering free personal protective equipment (PPE) packages to support spinal muscular atrophy (SMA) patients in the U.S. during the ongoing COVID-19 pandemic. Through the temporary program, called ... Read more

November 25, 2020November 25, 2020

Potential IPF Treatment, LYT-100, Shows Good Tolerability in Trial

COVID-19 News, Pulmonary Fibrosis News

Oral LYT-100 (deupirfenidone) was found to be safe and well-tolerated at all doses in an ongoing Phase 1 trial evaluating its potential to treat disorders involving inflammation and fibrosis, such ... Read more

November 24, 2020November 24, 2020

Gene Therapy Showing Efficacy Years After Use in Clinical Trials, Avrobio Says

COVID-19 News, Fabry Disease News

With data now reaching up to 3.5 years, benefits are continuing to be reported with the use of AVR-RD-01, Avrobio‘s experimental gene therapy for Fabry disease, in Phase 1 and 2 clinical trials, ... Read more

November 24, 2020November 24, 2020

PCF Helps Fund 2 Centers of Excellence to Treat Veterans With Prostate Cancer

COVID-19 News, Prostate Cancer News Today

The Prostate Cancer Foundation (PCF) has committed $5 million to support the launch of two new Centers of Excellence that will provide precision medicine treatments to veterans with prostate cancer. ... Read more

November 24, 2020November 24, 2020

App-Based Study Launched to Gain Better Understanding of Myasthenia Gravis

COVID-19 News, Myasthenia Gravis News

UCB Biopharma and doc.ai have launched a digital trial aimed at improving the speed and accuracy of diagnosis and predicting symptom flares in myasthenia gravis (MG) patients by recognizing vocal ... Read more

November 24, 2020November 24, 2020

Loneliness Linked to Worse Parkinson’s Symptoms, Study Finds

COVID-19 News, Parkinson's News Today

People with Parkinson’s disease who are lonely are more likely to have more severe symptoms and worse quality of life, a new study shows. The findings highlight the importance of ... Read more

November 23, 2020November 24, 2020

AVR-RD-02 Gene Therapy Lowers GD Biomarkers in First Patient Dosed in Trial

COVID-19 News, Gaucher Disease News

A single infusion of AVR-RD-02, Avrobio’s experimental gene therapy for Gaucher disease type 1, was able to lower the levels of two disease biomarkers within three months in the first ... Read more

November 23, 2020November 23, 2020

ChariotMS to Test Mavenclad in SPMS, PPMS Patients With Little Ability to Walk

COVID-19 News, Multiple Sclerosis News Today

An upcoming Phase 2 clinical trial, called ChariotMS, will test whether Mavenclad (cladribine) can slow a worsening of hand and arm function in people with progressive multiple sclerosis (MS) and ... Read more

November 23, 2020November 23, 2020

SpeechVive Offers Free, Remote Device-calibration Software During Pandemic

COVID-19 News, Parkinson's News Today

In response to the COVID-19 pandemic, SpeechVive is making remote calibration software and training free for its medical device — also called SpeechVive — which aims to help people with ... Read more

November 23, 2020November 23, 2020

1st Patient Enrolled in Trial Testing Ofev on Post-COVID-19 PF

COVID-19 News, Pulmonary Fibrosis News

The first patient has enrolled in a clinical trial to understand the effect of Ofev (nindetanib) on adults who developed pulmonary fibrosis (PF) following acute lung injury from COVID-19 infection. ... Read more

November 20, 2020November 20, 2020

Panhematin for AIP Deemed Essential Medicine By FDA

COVID-19 News, Porphyria News

Panhematin (hemin for injection), an approved medication to treat acute intermittent porphyria (AIP), has been deemed an essential medicine by the U.S. Food and Drug Administration (FDA), a designation intended ... Read more