COVID-19 News

July 28, 2021July 28, 2021

11-year-old With aHUS Patiently Waiting for a Kidney

aHUS News, COVID-19 News

On the outside, Khloe Sudol seems like a normal 11-year-old. The quiet, reserved girl is full of energy, filling her time with horseback riding, swimming, and school work. But on ... Read more

July 28, 2021July 28, 2021

FDA Greenlights Stem Cells Trial Aiming to Improve Quality of Life

COVID-19 News, Multiple Sclerosis News Today

The U.S. Food and Drug Administration (FDA) has given the green light to a Phase 2 clinical trial that will assess the efficacy of using adult mesenchymal stem cells (MSCs) to ... Read more

July 28, 2021July 28, 2021

AC Immune Acquires Experimental Vaccine PD01, Other Therapies

COVID-19 News, Parkinson's News Today

Parkinson’s vaccine candidate Affitope PD01, along with maker Affiris’ portfolio of other alpha-synuclein-targeting therapies, was acquired by AC Immune in a recent deal valued at nearly $60 million. “We believe ... Read more

July 27, 2021July 27, 2021

Rare Myopathy Affects Women, Too, Advocate Emphasizes

COVID-19 News, Muscular Dystrophy News

After being diagnosed as a carrier of x-linked myotubular myopathy (XLMTM) and losing her infant twin boys to the disease, Ashley Walker was driven into an episode of alcoholism. What ... Read more

July 27, 2021July 27, 2021

Rituximab Safe, Effective in Case of Sjogren’s-related ILD

COVID-19 News, Sjogren's Syndrome News

Rituximab safely and effectively treated sudden interstitial lung disease (ILD) in a 49-year-old man with undiagnosed primary Sjögren’s syndrome, a case study shows. This case adds to a growing number ... Read more

July 27, 2021July 27, 2021

Every ALS Patient in New Jersey to Get Free Eye Gaze Technology

ALS News Today, COVID-19 News

Thanks to a new partnership, every amyotrophic lateral sclerosis (ALS) patient in New Jersey, about 400 in total, will have free access to eye gaze technology that can aid them ... Read more

July 26, 2021July 26, 2021

R-107 Stops PAH Progression, Reverses Hypertension in Rats

COVID-19 News, Pulmonary Hypertension News

An investigational therapy called R-107 completely stopped the progression of pulmonary arterial hypertension (PAH) in a rat model and may become the first medicine to reverse the increasing blood pressure ... Read more

July 26, 2021July 26, 2021

PF Diagnosis, Care in UK Also Fell to COVID-19 Pandemic

COVID-19 News, Pulmonary Fibrosis News

More than 100,000 fewer hospital appointments were logged by people with lung diseases like idiopathic pulmonary fibrosis (IPF) in England between March 2020 and 2021, relative to the average annual ... Read more

July 26, 2021July 26, 2021

Gilenya Started Earlier in RRMS Disease Course in Recent Years

COVID-19 News, Multiple Sclerosis News Today

People with relapsing-remitting multiple sclerosis (RRMS) have switched to treatment with Gilenya (fingolimod) at an earlier stage in their disease in recent years, compared to individuals who switched to the ... Read more

July 23, 2021July 23, 2021

Digital Technology Changing Parkinson’s Research, Clinical Care

COVID-19 News, Parkinson's News Today

Digital health technology, which spans phone apps to telemedicine, is advancing Parkinson’s disease research and clinical care, according to different review studies. “Digital health technology is an important and promising ... Read more

July 23, 2021July 23, 2021

Speakers’ Bureau of 14 ‘Experts’ Living With Sarcoidosis Opens at FSR

COVID-19 News, Sarcoidosis News

A Patient Speakers’ Bureau is opening at the Foundation for Sarcoidosis Research (FSR) to advocate on behalf of people with this rare disease of the immune system and bring greater awareness to ... Read more

July 22, 2021July 22, 2021

EndFA’s Mobile App Aims to Unite FA Community, ‘Power the Cure’

COVID-19 News, Friedreich's Ataxia News

The nonprofit EndFA has launched a free mobile phone and tablet app to help connect, empower, and better inform people with Friedrich’s ataxia (FA) wherever they live. With the mission to ... Read more

July 21, 2021July 21, 2021

Shape Therapeutics Raises $112M to Develop RNA-based Gene Therapies

COVID-19 News, Rett Syndrome News

Shape Therapeutics has raised $112 million in financing to support work into developing its portfolio of RNA technologies to potentially treat genetic diseases, including Rett syndrome. “We have witnessed the ... Read more

July 21, 2021July 21, 2021

Specific Fibroblast Cells Prevent Fibrosis in PF Mouse Model Study

COVID-19 News, Pulmonary Fibrosis News

A subset of fibroblasts that produce a protein called meflin in lung tissues taken from people with idiopathic pulmonary fibrosis (IPF) was found to prevent fibrosis, or tissue scarring, in ... Read more

July 20, 2021July 20, 2021

Ultomiris Helps Ease gMG Symptoms in Ongoing Phase 3 Trial

COVID-19 News, Myasthenia Gravis News

Ultomiris (ravulizumab-cwvz) rapidly and sustainably eased symptom severity in adults with generalized myasthenia gravis (gMG), according to top-line data from a Phase 3 trial. Alexion Pharmaceuticals, the therapy’s developer, now ... Read more