ALS News Today

June 21, 2021June 21, 2021

Most Caregivers Did Not Get Respite During Pandemic, UK Survey Says

Most unpaid caregivers in the U.K. have not had any breaks from their caregiving role during the COVID-19 pandemic, with nearly three-quarters reporting feeling exhausted, stressed, and anxious, according to ... Read more

June 21, 2021June 21, 2021

EveryLife Introduces First of Kind ‘Roadmap’ to ICD Codes

ALS News Today

To help patient advocacy leaders and their partners better understand how global health statistics codes — known as ICD codes — are assigned, updated, and revised in the U.S. health ... Read more

June 18, 2021June 18, 2021

Artist With ALS Finds Collaborator, Friend, to Paint Through Disease

ALS News Today, COVID-19 News

A gay 39-year-old entrepreneur from Mexico and a retired white football player-turned-bank-CEO in the early stages of amyotrophic lateral sclerosis (ALS) come from different places and are in different stages ... Read more

June 17, 2021June 21, 2021

Get Ready for NORD’s Patient and Family Forum, Set for June 26-27

ALS News Today, COVID-19 News

Those who wish to gain practical tools for living optimally with rare diseases are encouraged to attend the annual Living Rare Living Stronger Patient and Family Forum, hosted by the ... Read more

June 17, 2021June 17, 2021

Partnership Targets Gene-editing Therapies for Familial ALS

ALS News Today

CRISPR Therapeutics and Capsida Biotherapeutics have partnered to develop gene-editing therapies for familial amyotrophic lateral sclerosis (ALS) and Friedreich’s ataxia. Capsida specializes in designing virus-based means of delivering therapies to ... Read more

June 16, 2021June 16, 2021

Clene Readying for HEALEY Trial Results of CNM-Au8 in Slowing ALS

ALS News Today

Clene and its subsidiary Clene Nanomedicine are negotiating to increase their manufacturing capacity as they prepare to release findings — expected early next year — from a pivotal and enrolling Phase ... Read more

June 15, 2021June 15, 2021

Amylyx Seeks Approval in Canada of Lead Candidate AMX0035

ALS News Today

Amylyx Pharmaceuticals is seeking approval, in Canada, of its lead candidate AMX0035 for the treatment of amyotrophic lateral sclerosis (ALS). This regulatory submission “represents a significant milestone in our efforts to develop a new ... Read more

June 14, 2021June 14, 2021

Get Ready for NORD’s Patient and Family Forum, Set for June 26-27

ALS News Today, COVID-19 News

Those who wish to gain practical tools for living optimally with rare diseases are encouraged to attend the annual Living Rare Living Stronger Patient and Family Forum, hosted by the ... Read more

June 14, 2021June 14, 2021

Tau Levels in Spinal Fluid Possible Biomarker of ALS, Likely Progression

ALS News Today

Levels of the protein tau found in the cerebrospinal fluid (CSF) — the transparent liquid surrounding the brain and spinal cord — can help in diagnosing amyotrophic lateral sclerosis (ALS), a ... Read more

June 11, 2021June 11, 2021

Investigational RNA Molecule May Slow ALS Progression

ALS News Today

An investigational RNA molecule called an RNA aptamer halted the death of motor neurons and helped preserve motor function in a mouse model of amyotrophic lateral sclerosis (ALS). Further research is ... Read more

June 10, 2021June 10, 2021

Stem Cells from Fat Tissue Protect Motor Neurons in ALS Mice

ALS News Today

Stem cells derived from fat tissue significantly improved motor function and delayed disease onset by protecting motor neurons in a mouse model of amyotrophic lateral sclerosis (ALS), a study shows. ... Read more

June 9, 2021June 9, 2021

Spinogenix’s SPG302 Oral Therapy Named Orphan Drug by FDA

ALS News Today

The U.S. Food and Drug Administration (FDA) has awarded orphan drug designation to Spinogenix’s investigational oral molecule SPG302 for treating amyotrophic lateral sclerosis (ALS). Orphan drug status is granted by ... Read more

June 8, 2021June 8, 2021

$1M DOD Grant Supports AS-202 for Sporadic ALS

ALS News Today

AccuraStem has been awarded a $1 million grant from the U.S. Department of Defense (DOD) to advance AS-202, a potentially disease-modifying therapy for sporadic amyotrophic lateral sclerosis (ALS), according to ... Read more

June 7, 2021June 7, 2021

Rare 2030 Action Campaign Pushing for European Plan for Rare Diseases

ALS News Today

Eurordis opened a campaign, called Rare 2030 Action, that is seeking to establish a European action plan for rare diseases to ensure that none of the 30 million people in ... Read more

June 7, 2021June 7, 2021

Orphan Drug Status Sought for Ketamine as Potential ALS Therapy

ALS News Today

PharmaTher has filed an application with the U.S. Food and Drug Administration (FDA) requesting that ketamine be designated an orphan drug as a potential treatment of amyotrophic lateral sclerosis (ALS). Orphan ... Read more