Posts by: Patricia Inacio PhD

Amolyt Pharma has raised $80 million in financing that will support the clinical development of AZP-3601, its experimental therapy for hypoparathyroidism. Hypoparathyroidism is caused by abnormally low levels of the ... Read more

September 20, 2021September 20, 2021

AirPhysio Lung-cleaning Device Now Sold Online for U.S. Patients

Cystic Fibrosis News Today

AirPhysio, a handheld device designed to help clear the mucus that builds up in the lungs of people with cystic fibrosis (CF), is now available online in the U.S. through ... Read more

September 17, 2021September 18, 2021

$75M Funding Will Help TreeFrog Develop Stem Cell Therapies

Parkinson's News Today

TreeFrog Therapeutics has raised $75 million in financing to support the clinical development of its stem cell-derived cell therapies for Parkinson’s disease, the company said in a press release. The new ... Read more

September 17, 2021September 17, 2021

Post-surgery Use of Enoxaparin Lowered Blood Clot Risk

Cushing's Disease News

Treatment with the blood thinner enoxaparin within a few hours after curative pituitary surgery may help reduce the risk of blood clots forming in people with Cushing’s disease, a new ... Read more

September 17, 2021September 17, 2021

Trial of Spinraza at High Dose in SMA Patients Who Used Evrysdi Planned

SMA News Today

Biogen plans to launch ... Read more

September 16, 2021September 16, 2021

Dosing Begins in Phase 1 Trial of INV-102, Potential PWS Therapy

Prader-Willi News

The first healthy volunteers were dosed in a Phase 1 clinical trial evaluating Inversago Pharma‘s INV-102, a potential therapy for Prader-Willi syndrome (PWS) and other metabolic disorders. According to a ... Read more

September 16, 2021September 16, 2021

Emily’s Entourage Opens Its Philly Marathon Team to CF Community

Cystic Fibrosis News Today

A nonprofit’s entry in the Philadelphia Marathon, Team EE is looking for enthusiastic people to join it for the November race that will help to raise funds for the 10% ... Read more

September 16, 2021September 16, 2021

Roche, Temedica Launch Brisa App to Improve Lives of German Patients

Multiple Sclerosis News Today

Temedica, a Munich-based digital health company, has joined efforts with Roche to launch a free mobile app that aims to improve care for people with multiple sclerosis (MS) living in ... Read more

September 16, 2021September 16, 2021

Genetic Testing Costly, Hard to Access, Survey Shows

Parkinson's News Today

High prices, lack of access, and long waiting times are major barriers to people who want to undergo genetic testing for Parkinson’s disease, according to a survey by the International ... Read more

September 15, 2021September 15, 2021

Soliris Successfully Treats aHUS in COVID-19 Patient With Heart Transplant

aHUS News, COVID-19 News

Soliris (eculizumab) was shown to effectively treat atypical hemolytic uremic syndrome (aHUS) triggered by COVID-19 in a patient who had undergone a heart transplant five years earlier, according to a ... Read more

September 15, 2021September 15, 2021

No Need for Nausea Treatment for Most Patients on Kynmobi

Parkinson's News Today

The majority of Parkinson’s patients given Sunovion‘s Kynmobi (apomorphine hydrochloride) for “off” episodes during Phase 3 clinical trials did not require additional treatment for vomiting or nausea, the company said. ... Read more

September 15, 2021September 15, 2021

OSIC Opens Large Database to Aid Research Into PF, Other ILDs

Pulmonary Fibrosis News

A large and multi-ethnic database, reported to be the first of its kind for rare lung diseases, is now compiling real-world clinical and imaging data on people with pulmonary fibrosis ... Read more

September 14, 2021September 14, 2021

10th SCD Therapeutics Conference on Sept. 15 to Focus on Advances

COVID-19 News, Sickle Cell Disease News

The 10th Annual Sickle Cell Disease Therapeutics Conference, to be held virtually Sept. 15, will highlight the most recent medical advances and developing treatment trends in the field of sickle ... Read more

September 14, 2021September 14, 2021

CDNF, Potential DMT for Parkinson’s, May Work as Nasal Spray

Parkinson's News Today

A potential Parkinson’s therapy based on a protein with an ability to protect neurons — called recombinant (lab-made) human cerebral dopamine neurotrophic factor (rhCDNF) — has been transformed into tiny nanoparticles that may allow for ... Read more

September 13, 2021September 13, 2021

Risk of COPD 30% Higher in Earliest Responders to Twin Towers Collapse

COPD News Today

Twenty years after the collapse the World Trade Center, rescue workers and volunteers who assisted at the site in the two days that immediately followed face a 30% increased risk ... Read more