Posts by: Patricia Inacio PhD

Gosuranemab, an investigational antibody against the tau protein, failed to meet its primary and exploratory efficacy goals in the TANGO Phase 2 study, its developer, Biogen, has announced. Now, the TANGO ... Read more

June 21, 2021June 21, 2021

Israel Agrees to Review BioCryst’s Marketing Request for Orladeyo

Angioedema News

The Israeli Ministry of Health has agreed to review, under an accelerated process, a marketing application for Orladeyo (berotralstat), BioCryst Pharmaceuticals’ oral preventive treatment for hereditary angioedema (HAE) attacks, in patients ... Read more

June 21, 2021June 21, 2021

Poorer Joint Health, Greater Pain Evident After COVID Lockdown

COVID-19 News, Hemophilia News Today

Joint pain significantly rose and overall joint health — particularly range of motion — diminished with limitations on physical activities during the COVID-19 lockdown for people with hemophilia and joint disease, a ... Read more

June 21, 2021June 21, 2021

First Patient Treated in Study Testing Aleva’s directSTIM DBS System

Parkinson's News Today

Aleva Neurotherapeutic’s innovative directional deep brain stimulation (DBS) system — called directSTIM — for Parkinson’s disease has been implanted in the first patient participating in a German study. That study, ... Read more

June 18, 2021June 18, 2021

Study Examines Inhibitor Risk in Non-severe Hemophilia A

Hemophilia News Today

Intensive treatment with factor VIII, the clotting protein missing or defective in patients with hemophilia A, is associated with a greater risk of inhibitor development among patients with non-severe disease, ... Read more

June 17, 2021June 17, 2021

Ruconest for Acute HAE Attacks Now Reimbursable in Spain

Angioedema News

Spain has added Ruconest (conestat alfa), Pharming’s treatment for acute attacks of hereditary angioedema (HAE), to its list of reimbursable medications. “We are delighted with this positive reimbursement decision by the ... Read more

June 16, 2021June 16, 2021

Clene Readying for HEALEY Trial Results of CNM-Au8 in Slowing ALS

ALS News Today

Clene and its subsidiary Clene Nanomedicine are negotiating to increase their manufacturing capacity as they prepare to release findings — expected early next year — from a pivotal and enrolling Phase ... Read more

June 15, 2021June 15, 2021

Home-based Exercise Viable Alternative for RRMS Patients

Multiple Sclerosis News Today

A home-based rehabilitation program can help ease fatigue, improve motor and cognitive function, and promote better quality of life in people with relapsing-remitting multiple sclerosis (RRMS), a small clinical trial ... Read more

June 14, 2021June 14, 2021

Shepherd Center, BurnAlong Open Global Online Rehab Classes for MS

Multiple Sclerosis News Today

BurnAlong and the Shepherd Center, a leading rehabilitation hospital in the U.S., have established a partnership to bring tailored rehabilitation classes to people with multiple sclerosis (MS) and other neuromuscular diseases worldwide. ... Read more

June 14, 2021June 14, 2021

Prostacyclin Therapy, Expert Care Help in Pregnancy With PAH

Pulmonary Hypertension News

Despite a high-risk of serious complications, 10 women with moderate to severe pulmonary arterial hypertension (PAH) had a successful pregnancy and delivery, according to a single center study. The patients ... Read more

June 11, 2021June 11, 2021

Investigational RNA Molecule May Slow ALS Progression

ALS News Today

An investigational RNA molecule called an RNA aptamer halted the death of motor neurons and helped preserve motor function in a mouse model of amyotrophic lateral sclerosis (ALS). Further research is ... Read more

June 11, 2021June 11, 2021

Stem Cell Transplant Trial Enrolls First Patient in Minnesota

Multiple Sclerosis News Today

A clinical trial investigating patient-derived stem cell transplants for the treatment of people with severe relapsing forms of multiple sclerosis (MS) has enrolled a patient in Minnesota. The patient was ... Read more

June 10, 2021June 10, 2021

ANVS401 Improves Cognition in Alzheimer’s and Parkinson’s, Data Show

Alzheimer's News Today, COVID-19 News

Annovis Bio’s oral therapy ANVS401 (also known as Posiphen) led to significant improvements in cognition in patients with Alzheimer’s disease, according to data from the first patient group in a ... Read more

June 9, 2021June 9, 2021

Disc Medicine Buys Global Rights to Potential Oral Therapy for EPP

Porphyria News

Disc Medicine has entered into an exclusive worldwide licensing agreement to develop and commercialize Roche’s bitopertin, an oral candidate therapy for blood disorders. Disc will initially develop bitopertin for erythropoietic ... Read more

June 9, 2021June 9, 2021

Spinogenix’s SPG302 Oral Therapy Named Orphan Drug by FDA

ALS News Today

The U.S. Food and Drug Administration (FDA) has awarded orphan drug designation to Spinogenix’s investigational oral molecule SPG302 for treating amyotrophic lateral sclerosis (ALS). Orphan drug status is granted by ... Read more