Posts by: Marta Figueiredo PhD

Hospitalizations for chronic obstructive pulmonary disease (COPD) dropped by half after the implementation of public health measures to curb the spread of COVID-19 infections, according to a U.S. study. This ... Read more

June 21, 2021June 21, 2021

Most Caregivers Did Not Get Respite During Pandemic, UK Survey Says

ALS News Today, COVID-19 News

Most unpaid caregivers in the U.K. have not had any breaks from their caregiving role during the COVID-19 pandemic, with nearly three-quarters reporting feeling exhausted, stressed, and anxious, according to ... Read more

June 21, 2021June 21, 2021

Newborn Screening in Massachusetts Seen as Highly Accurate, Effective

SMA News Today

Newborn screening (NBS) for spinal muscular atrophy (SMA) in Massachusetts allowed for early detection and treatment of affected infants, with most referred to a specialist within the first week of life, ... Read more

June 18, 2021June 18, 2021

Dietary App May Help CF Patients in Meeting Nutritional Needs

Cystic Fibrosis News Today

A mobile, dietary self-monitoring app used for six months to track food choices and manage pancreatic enzyme replacement therapy (PERT) helped children with cystic fibrosis (CF) to better meet disease-specific ... Read more

June 18, 2021June 18, 2021

Brainstorm Secures NurOwn-associated Patents in Several Markets

Multiple Sclerosis News Today

In the past year, BrainStorm Cell Therapeutics was granted four patents and is waiting for a fifth, already accepted, meant to provide protection for its NurOwn cell therapy and technology ... Read more

June 18, 2021June 18, 2021

Mechanisms Behind Anavex 2-73’s Benefits Highlighted in Review

Alzheimer's News Today

Activation of the sigma-1 receptor or SIGMAR1 — whose production is typically increased with age, but reduced in people with Alzheimer’s disease — drives a series of neuroprotective effects, including ... Read more

June 18, 2021June 18, 2021

Simple Reading Task May Help Detect Early Disease

Parkinson's News Today

Assessing vowel percentage, or duration, during a simple reading task is an effective method to detect changes in speech rhythm at early stages of Parkinson’s disease, according to a small ... Read more

June 17, 2021June 17, 2021

Brineura Delays CLN2 Onset, Progression in Case Study of 2 Siblings

Batten Disease News

Two years of treatment with Brineura (cerliponase alfa) safely and effectively delayed the onset of late-infantile Batten disease in a 23-month-old boy who had not exhibited symptoms when he started ... Read more

June 17, 2021June 17, 2021

Oxbryta in HOPE-KIDS Meeting ‘Urgent Need’ of Children, Ages 4-11

Sickle Cell Disease News

In children with sickle cell disease (SCD), ages 4–11, weight-based doses of Oxbryta (voxelotor) result in similar rises in hemoglobin levels and reductions in red blood cell destruction (hemolysis) to ... Read more

June 16, 2021June 16, 2021

Research Sheds Light on Potential Immune Changes in IPAH

Pulmonary Hypertension News

A combination of lung injury and increased activation of B-cells — immune cells responsible for antibody production — was sufficient to promote symptoms of pulmonary hypertension (PH) in mice, a study ... Read more

June 16, 2021June 16, 2021

Asymmetric Loss of Brain Neurons Tied to Different Symptom Severity

Parkinson's News Today

The asymmetric loss of dopamine-producing, or dopaminergic, neurons in the brains of people with Parkinson’s disease may determine the severity of patients’ motor and cognitive symptoms, a study suggests. Such ... Read more

June 15, 2021June 15, 2021

UK Gives Eligible Late-onset Pompe Patients Early Access to AT-GAA

Pompe Disease News

AT-GAA, an investigational therapy by Amicus Therapeutics for late-onset Pompe disease, will be available to select patients in the U.K. through an early access program before its potential regulatory approval. ... Read more

June 15, 2021June 15, 2021

Amylyx Seeks Approval in Canada of Lead Candidate AMX0035

ALS News Today

Amylyx Pharmaceuticals is seeking approval, in Canada, of its lead candidate AMX0035 for the treatment of amyotrophic lateral sclerosis (ALS). This regulatory submission “represents a significant milestone in our efforts to develop a new ... Read more

June 15, 2021June 15, 2021

Apomorphine as Steady Infusion of Benefit in Advanced Parkinson’s

Parkinson's News Today

Two years of continuous treatment with apomorphine as an under-the-skin infusion safely preserved quality of life and effectively eased motor fluctuations in people with advanced Parkinson’s disease, according to a single-center, real-life study in ... Read more

June 14, 2021June 14, 2021

Oral PHA121 May Lead to Faster, More Durable Effects Than Firazyr

Angioedema News

PHA121 (PHA-022121), Pharvaris’ experimental oral therapy for hereditary angioedema (HAE), results in faster, more potent, and more durable suppression of bradykinin-induced changes in blood pressure than injectable Firazyr (icatibant), according ... Read more