US Medical Data Show Higher Mortality in SMA Patients Before DMT Era

US Medical Data Show Higher Mortality in SMA Patients Before DMT Era

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US Medical Data Show Higher Mortality in SMA Patients Before DMT Era

Before the emergence of Spinraza (nusinersen) — the first disease-modifying therapy (DMT) approved for spinal muscular atrophy (SMA) — patients of all ages and types of the disease showed greater all-cause mortality than their peers who did not have SMA and the general population, according to a large study based on U.S. medical records. These findings highlight that even those with type 3, a milder later-onset form of SMA thought to be associated with normal…

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