Sanfilippo Ideal for FDA’s Accelerated Approval Pathway, Foundation Says

Sanfilippo Ideal for FDA’s Accelerated Approval Pathway, Foundation Says

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Sanfilippo Ideal for FDA’s Accelerated Approval Pathway, Foundation Says

The Cure Sanfilippo Foundation is encouraging the U.S. Food & Drug Administration (FDA) to consider Sanfilippo syndrome as a candidate for the agency’s accelerated approval pathway. According to a recent foundation-led study, families of Sanfilippo children are willing to accept modest treatment benefits even if they come with risks. “Doing nothing is the biggest risk in Sanfilippo!” Glenn O’Neill, foundation president and father to a Sanfilippo child, said in a press release. His statement came…

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