Elamipretide as Add-on May Boost Efficacy of Exon-skipping Therapies

Elamipretide as Add-on May Boost Efficacy of Exon-skipping Therapies

314340

Elamipretide as Add-on May Boost Efficacy of Exon-skipping Therapies

Elamipretide, an investigational therapy designed to increase the activity of mitochondria, may boost the effectiveness of exon-skipping therapies for Duchenne muscular dystrophy (DMD), its developer, Stealth BioTherapeutics, reported. “Our new preclinical data increases our optimism that elamipretide may help address the unmet need for therapies in DMD,” Reenie McCarthy, the CEO of Stealth, said in a press release. Mitochondria are often referred to as the “powerhouses of the cell,” because they are critical for energy generation.…

You must be logged in to read/download the full post.