Translarna Preserved Walking 5-plus Years in DMD Boys

Translarna Preserved Walking 5-plus Years in DMD Boys

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Translarna Preserved Walking 5-plus Years in DMD Boys

Translarna (ataluren) treatment delayed the loss of walking abilities by more than five years in boys with Duchenne muscular dystrophy (DMD) who carry nonsense mutations in their DMD gene, according to a study based on real-world data. The investigational therapy also slowed lung function decline by almost two years. These most recent findings from the STRIDE registry — an ongoing, observational and international study — were presented at the World Muscle Society (WMS) 2021 Virtual Congress,…

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