Certain Abilities Decline in SMA Type 3 Children Unable to Walk

Certain Abilities Decline in SMA Type 3 Children Unable to Walk

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Certain Abilities Decline in SMA Type 3 Children Unable to Walk

Lung function and upper limb abilities worsened over a two-year period in young people with spinal muscular atrophy (SMA) type 3 who were unable to walk (non-ambulatory), a U.K. study has found. At the time of the study, the approved, disease-modifying therapy Spinraza (nusinersen) was unavailable to SMA type 3 patients in the U.K. who had lost their ability to walk for more than one year, which included the patients in this study, the researchers…

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