Small Molecules, STARs Treat Cell Models of GBA1-linked Parkinson’s

Small Molecules, STARs Treat Cell Models of GBA1-linked Parkinson’s

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Small Molecules, STARs Treat Cell Models of GBA1-linked Parkinson’s

Two investigational small molecules known as GT-02287 and GT-02329 lowered toxic protein levels in patient-derived cell models of Parkinson’s disease associated with a mutation in GBA1, their developer, Gain Therapeutics, announced. Gain is planning additional preclinical studies this year that could support applications to regulatory agencies allowing the compounds to be tested in people, the company’s CEO, Eric Richman, said in a press release. “These data are extremely exciting, as it further demonstrates the potential of GT-02287…

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