CRISPR Gene Editing Therapy Is Promising in New Mixed Model

CRISPR Gene Editing Therapy Is Promising in New Mixed Model

295370

CRISPR Gene Editing Therapy Is Promising in New Mixed Model

A CRISPR-Cas9-based gene editing therapy promoted the production of a smaller but functional version of the dystrophin protein in a new mixed mouse model that uses muscle cells derived from Duchenne muscular dystrophy (DMD) patients. The therapy is designed to delete a DMD gene region that is commonly mutated in people with DMD. This is one of the first studies to prove the efficacy of this type of gene editing therapy in adult cells within a living organism,…

You must be logged in to read/download the full post.