Gene Therapy Trial for Rare Form of MD Planned for Next Year

Gene Therapy Trial for Rare Form of MD Planned for Next Year

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Gene Therapy Trial for Rare Form of MD Planned for Next Year

Asklepios BioPharmaceutical (AskBio) is planning to launch a Phase 1/2 clinical study to evaluate LION-101, its investigational gene therapy for limb-girdle muscular dystrophy type 2I/R9 (LGMD2I/R9). Dosing in the trial is expected to start in the first half of next year. “We are excited to begin clinical trials with this novel therapy, and to hopefully bring a new therapeutic option to patients and families in the LGMD2I/R9 community,” Katherine High, MD, president of therapeutics at…

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