New Study Explores Variability in ERT Outcomes

New Study Explores Variability in ERT Outcomes

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New Study Explores Variability in ERT Outcomes

Enzyme replacement therapy (ERT) may not effectively manage all aspects of Fabry disease in all patients, particularly when started at more advanced ages, a new study indicates. The findings highlight the need to start treatment early, its researchers said. The study, “Variable clinical features of patients with Fabry disease and outcome of enzyme replacement therapy,” was published in Molecular Genetics and Metabolism Reports. Fabry disease is caused by a lack of alpha-galactosidase A, due to mutations in…

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