Criteria for Gene Therapy Trials Can Exclude Many With Severe Hemophilia

Criteria for Gene Therapy Trials Can Exclude Many With Severe Hemophilia

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Criteria for Gene Therapy Trials Can Exclude Many With Severe Hemophilia

Screening for clinical trials in gene therapy can exclude the vast majority — 92% — of severe hemophilia patients, for reasons too often due to potentially modifiable factors such as socioeconomic status and location, a study of patients at a treatment center in Belgium reported. Patients’ unwillingness to take part in a gene therapy study was also a factor, but individual hesitancy and trial eligibility criteria should change as gene therapies become more widely accepted, and possibly…

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