#AANAM – Gene Therapy Shows Promise in Early Type A Disease

#AANAM – Gene Therapy Shows Promise in Early Type A Disease

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#AANAM – Gene Therapy Shows Promise in Early Type A Disease

Treatment with ABO-102, an investigational gene therapy being developed by Abeona Therapeutics, normalized development in children with Sanfilippo syndrome type A, according to new data from a clinical trial. The data indicate that the gene therapy is especially effective when given early in life, before the disease has started to progress. The findings were presented at the 2021 annual meeting of the American Academy of Neurology in a talk, titled “Results of Transpher A, a…

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