#AANAM – PTC-AADC Gene Therapy Found to Improve Patient Motor Function

#AANAM – PTC-AADC Gene Therapy Found to Improve Patient Motor Function

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#AANAM – PTC-AADC Gene Therapy Found to Improve Patient Motor Function

The investigational gene therapy PTC-AADC improved motor function in children with aromatic l-amino acid decarboxylase (AADC) deficiency in several clinical studies, new data show. These findings were presented at this year’s American Academy of Neurology annual meeting by Mark Pykett, PhD, the chief scientific officer of PTC Therapeutics, which is developing PTC-AADC and helped fund the studies. The AAN virtual meeting is being held online April 17-22. AADC deficiency is caused by mutations in the…

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