A ‘Miracle’: Spinraza Gives Boy, Now 5, a Chance to Grow Up

A ‘Miracle’: Spinraza Gives Boy, Now 5, a Chance to Grow Up

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A ‘Miracle’: Spinraza Gives Boy, Now 5, a Chance to Grow Up

It’s now been more than four years since Spinraza (nusinersen) was first approved by the U.S. Food and Drug Administration, and presymptomatic children with spinal muscular atrophy (SMA) who received therapy as part of the Phase 2 NURTURE trial are growing up fast and, by all accounts, showing good progress. Jase Yoder, 5, is one of those children. He was featured as part of “The Gene” documentary on PBS last year. In the segment, Jase,…

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