Better Ways of Capturing Progression in Types 2 and 3 Identified in Study

Better Ways of Capturing Progression in Types 2 and 3 Identified in Study

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Better Ways of Capturing Progression in Types 2 and 3 Identified in Study

Four measures of motor ability — including one of continuous upper limb activity that can be done at the home — reliably detect significant functional changes over one or two years in people with spinal muscular atrophy (SMA) types 2 and 3, according to a natural history study. These findings support the use of such measures in future clinical trials to better evaluate disease progression in these patients, and to strengthen a trial’s likelihood of…

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