PTC Preparing to Launch Gene Therapy, Pending Approval

PTC Preparing to Launch Gene Therapy, Pending Approval

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PTC Preparing to Launch Gene Therapy, Pending Approval

PTC Therapeutics is preparing to launch PTC-AADC, its experimental gene therapy for aromatic l-amino acid decarboxylase (AADC) deficiency, the company has announced in a press release. Among other launch efforts, the company is expanding its genetic testing program, while finding and preparing expert pediatric neurosurgical centers. AADC deficiency is a genetic disorder caused by mutations in the DDC gene, which codes for the AADC enzyme, required to produce two neurotransmitters — chemical messengers used by nerve…

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