Non-viral Gene Therapy Shows Promise in Hemophilia A Animal Models

Non-viral Gene Therapy Shows Promise in Hemophilia A Animal Models

282020

Non-viral Gene Therapy Shows Promise in Hemophilia A Animal Models

Generation Bio has announced new data showing that its investigational non-viral gene therapy platform can increase levels of the clotting protein factor VIII (FVIII) in mouse and non-human primate models of hemophilia A. The data support the selection of a final candidate therapy for clinical development later this year, the company said in a press release. Hemophilia A is caused by missing or defective FVIII due to mutations in the gene that provides instructions to…

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